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| EWTX | Edgewise Therapeutics, Inc. | $38.33 | $4.1B |
| GPCR | Structure Therapeutics Inc. | $50.41 | $2.9B |
| QURE | uniQure N.V. | $40.38 | $2.7B |
| NUVB | Nuvation Bio Inc. | $6.55 | $2.3B |
| MESO | Mesoblast Limited | $16.30 | $2.1B |
| HRMY | Harmony Biosciences Holdings, Inc. | $34.86 | $2.0B |
| AUPH | Aurinia Pharmaceuticals Inc. | $15.33 | $2.0B |
| OCUL | Ocular Therapeutix, Inc. | $8.59 | $1.9B |
| VRDN | Viridian Therapeutics, Inc. | $19.17 | $1.7B |
| MNKD | MannKind Corporation | $3.84 | $1.2B |