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| PRAX | Praxis Precision Medicines, Inc. | $351.81 | $9.8B |
| BLTE | Belite Bio, Inc | $193.61 | $7.8B |
| MIRM | Mirum Pharmaceuticals, Inc. | $100.90 | $6.2B |
| LGND | Ligand Pharmaceuticals Incorporated | $285.60 | $5.7B |
| ACAD | ACADIA Pharmaceuticals Inc. | $28.02 | $4.8B |
| CELC | Celcuity Inc. | $95.70 | $4.7B |
| DYN | Dyne Therapeutics, Inc. | $24.28 | $4.5B |
| SLNO | Soleno Therapeutics, Inc. | $53.01 | $2.8B |
| ADMA | ADMA Biologics, Inc. | $9.62 | $2.2B |
| RARE | Ultragenyx Pharmaceutical Inc. | $15.30 | $1.5B |