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| KNSA | Kiniksa Pharmaceuticals International, plc | $76.48 | $5.8B |
| XENE | Xenon Pharmaceuticals Inc. | $58.80 | $5.7B |
| CDTX | Cidara Therapeutics, Inc. | $221.38 | $5.6B |
| ADPT | Adaptive Biotechnologies Corporation | $24.23 | $3.9B |
| IDYA | IDEAYA Biosciences, Inc. | $37.45 | $3.6B |
| LEGN | Legend Biotech Corporation | $19.19 | $3.5B |
| IRON | Disc Medicine, Inc. | $74.14 | $2.8B |
| ZLAB | Zai Lab Limited | $24.17 | $2.7B |
| MLYS | Mineralys Therapeutics, Inc. | $29.30 | $2.6B |
| BEAM | Beam Therapeutics Inc. | $24.37 | $2.5B |