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| MDGLMDGLMadrigal Pharmaceuticals, Inc. | Madrigal Pharmaceuticals, Inc. | $434.24 | $10.0B |
| TVTXTVTXTravere Therapeutics, Inc. | Travere Therapeutics, Inc. | $50.08 | $4.7B |
| AGIOAGIOAgios Pharmaceuticals, Inc. | Agios Pharmaceuticals, Inc. | $37.00 | $2.2B |
| RARERAREUltragenyx Pharmaceutical Inc. | Ultragenyx Pharmaceutical Inc. | $15.95 | $1.6B |
| ALTALTAltimmune, Inc. | Altimmune, Inc. | $2.12 | $412.4M |
| ENTAENTAEnanta Pharmaceuticals, Inc. | Enanta Pharmaceuticals, Inc. | $11.64 | $339.0M |
| ARCTARCTArcturus Therapeutics Holdings Inc. | Arcturus Therapeutics Holdings Inc. | $9.84 | $279.7M |