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| PRAX | Praxis Precision Medicines, Inc. | $334.58 | $9.3B |
| CRNX | Crinetics Pharmaceuticals, Inc. | $84.95 | $9.0B |
| BLTE | Belite Bio, Inc | $173.79 | $7.0B |
| MIRM | Mirum Pharmaceuticals, Inc. | $98.22 | $6.0B |
| ACAD | ACADIA Pharmaceuticals Inc. | $27.83 | $4.8B |
| VKTX | Viking Therapeutics, Inc. | $31.98 | $3.7B |
| DYN | Dyne Therapeutics, Inc. | $18.21 | $3.4B |
| SLNO | Soleno Therapeutics, Inc. | $53.01 | $2.8B |
| NAMS | NewAmsterdam Pharma Company N.V. | $22.80 | $2.7B |
| ADMA | ADMA Biologics, Inc. | $9.23 | $2.1B |