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| MGTXMGTXMeiraGTx Holdings plc | MeiraGTx Holdings plc | $9.40 | $902.8M |
| SANASANASana Biotechnology, Inc. | Sana Biotechnology, Inc. | $2.47 | $739.4M |
| RGNXRGNXREGENXBIO Inc. | REGENXBIO Inc. | $6.60 | $435.7M |
| RCKTRCKTRocket Pharmaceuticals, Inc. | Rocket Pharmaceuticals, Inc. | $2.45 | $268.9M |
| ABEOABEOAbeona Therapeutics Inc. | Abeona Therapeutics Inc. | $4.31 | $246.5M |