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| UTHRUTHRUnited Therapeutics Corporation | United Therapeutics Corporation | $587.50 | $25.2B |
| INSMINSMInsmed Incorporated | Insmed Incorporated | $93.39 | $20.4B |
| NBIXNBIXNeurocrine Biosciences, Inc. | Neurocrine Biosciences, Inc. | $142.70 | $14.5B |
| BMRNBMRNBioMarin Pharmaceutical Inc. | BioMarin Pharmaceutical Inc. | $55.95 | $10.8B |
| CORTCORTCorcept Therapeutics Incorporated | Corcept Therapeutics Incorporated | $85.86 | $9.3B |
| MBXMBXMBX Biosciences, Inc. Common Stock | MBX Biosciences, Inc. Common Stock | $48.50 | $2.3B |
| SEPNSEPNSepterna Inc | Septerna Inc | $40.41 | $1.9B |
| XERSXERSXeris Biopharma Holdings, Inc. | Xeris Biopharma Holdings, Inc. | $10.20 | $1.9B |
| STOKSTOKStoke Therapeutics, Inc. | Stoke Therapeutics, Inc. | $25.04 | $1.6B |
| RARERAREUltragenyx Pharmaceutical Inc. | Ultragenyx Pharmaceutical Inc. | $15.65 | $1.5B |