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| SRRK | Scholar Rock Holding Corporation | $54.62 | $6.5B |
| CDTX | Cidara Therapeutics, Inc. | $221.38 | $5.6B |
| CPRX | Catalyst Pharmaceuticals, Inc. | $31.49 | $3.9B |
| LEGN | Legend Biotech Corporation | $19.91 | $3.7B |
| IDYA | IDEAYA Biosciences, Inc. | $38.35 | $3.6B |
| TARS | Tarsus Pharmaceuticals, Inc. | $82.77 | $3.6B |
| IRON | Disc Medicine, Inc. | $76.51 | $2.9B |
| ZLAB | Zai Lab Limited | $25.08 | $2.8B |
| MLYS | Mineralys Therapeutics, Inc. | $30.50 | $2.7B |
| BEAM | Beam Therapeutics Inc. | $25.18 | $2.6B |